New Look, Same Mission!

In April 2022, Children’s Hospital of Pittsburgh Foundation officially became UPMC Children’s Hospital Foundation! 

Innovation in Gene Therapy Starts at UPMC Children’s

UPMC Children’s is on its way to becoming the lead site for development and human clinical trials of a new gene therapy treatment for VLCADD (Very Long Chain Acyl CoA Dehydrogenase Deficiency), a rare genetic disorder that is identified through newborn screening.